Drug
Ctx001
Ctx001: highest development phase Phase 3, developed by Vertex Pharmaceuticals. 4 trial records tracked on RxWires.
- Highest phase
- Phase 3
- Developer
- Vertex Pharmaceuticals
Trials
| Drug | Phase | Indication |
|---|---|---|
| CTX001 NCT05356195 | Phase 3 | Beta-Thalassemia |
| CTX001 NCT05329649 | Phase 3 | Sickle Cell Disease |
| CTX001 NCT04208529 | Phase 3 | Beta-Thalassemia |
| CTX001 NCT03655678 | Phase 2/3 | Beta-Thalassemia |
Latest
No recent events.
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Sourced from ClinicalTrials.gov, openFDA, SEC EDGAR and the FDA Orange Book. Not investment or medical advice.